Investigating Therapeutic Discovery Platforms for Oligonucleotides Targeting Neurodegenerative Diseases

Time: 1:03 pm
day: Pre-Conference Discussion Day


  • High-throughput, high information content platform to study the function of neurons with single cell and single action potential resolution
  • Using AI/ML-based analyses to identify neuronal phenotypes to assess performance characteristics of therapeutic antisense oligonucleotides (ASOs)
  • Developing ASOs for genetically defined neurodegenerative diseases